A new type of genetically engineered lab-grown cell may help researchers determine whether certain genetic variants can contribute to Alagille syndrome, a study reports.
Alagille syndrome
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Alagille syndrome is a genetic disease that can cause a wide range of symptoms, typically including liver problems as well as heart issues and characteristic changes in the shape of the face.
A range of treatment options, including medications and surgical procedures, are available for managing Alagille syndrome symptoms and improving quality of life for patients
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As a dad, I enjoy seeing my sons figure out what interests them. I have two boys — Jackson, 8, and Finley, 5 — and…
Treatment with Livmarli (maralixibat) can reduce cholesterol levels and help clear fatty skin growths called xanthomas in children with Alagille syndrome, according to…
