A liver transplant with an uncle serving as a living donor successfully managed advanced progressive familial intrahepatic cholestasis type 2 (PFIC2) in a one-year-old…

With new support from the U.S. Food and Drug Administration (FDA), Galectin Therapeutics is preparing for a late-stage clinical trial to test its therapy…

One thing that’s important to me as a parent raising a child with a rare genetic condition is to be able to help share the…